Zolgensma: A Cure For Spinal Muscular Atrophy

Zolgensma: A Cure For Spinal Muscular Atrophy

The first of its kind, Zolgensma, received FDA approval for a single dose administered therapy that uses the protein capsule of adeno-virus with double stranded complementary gene therapy implanted inside, intended to cure spinal muscular atrophy type 1, a genetic...